LATORRE, ROBERTA VALERIA

LATORRE, ROBERTA VALERIA  

DIPARTIMENTO DI MEDICINA  

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Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids 1-gen-2025 Nicosia, Lucia; Pranke, Iwona; Latorre, Roberta V.; Murray, Joss B.; Lonetti, Lisa; Cavusoglu-Doran, Kader; Dreano, Elise; Costello, James P.; Carroll, Michael; Melotti, Paola; Sorio, Claudio; Sermet-Gaudelus, Isabelle; Scallan, Martina F.; Harrison, Patrick T.
Autoreactivity to self-antigens LL37 and ADAMTSL5 influences the clinical response to risankizumab in psoriatic patients 1-gen-2024 Favaro, Rebecca; Facheris, Paola; Formai, Alessandra; Gargiulo, Luigi; Ibba, Luciano; Fiorillo, Giovanni; Latorre, ROBERTA VALERIA; Avagliano, Jessica; Narcisi, Alessandra; Girolomoni, Giampiero; Raffaele Mercuri, Santo; Costanzo, Antonio
CFTR Modulators Rescue the Activity of CFTR in Colonoids Expressing the Complex Allele p.[R74W;V201M;D1270N]/dele22_24 1-gen-2023 Kleinfelder, Karina; Somenza, Elena; Farinazzo, Alessia; Conti, Jessica; Lotti, Virginia; Latorre, ROBERTA VALERIA; Rodella, Luca; Massella, Arianna; Tomba, Francesco; Bertini, Marina; Sorio, Claudio; Melotti, Paola
Evaluation of the response to elexacaftor-tezacaftor-ivacaftor of the rare CFTR variants L383S, I507del, L1065P and R1066H in intestinal organoid-derived epithelial monolayers 1-gen-2025 Conti, Jessica; Angyal, Dora; Kleinfelder, Karina; Latorre, Roberta Valeria; Calicchia, Martina; Farinazzo, Alessia; Rodella, Luca; Tomba, Francesco; Massella, Arianna; Frulloni, Luca; Taccetti, Giovanni; Terlizzi, Vito; Leung, Anny; Groeneweg, Tessa A.; Bijvelds, Marcel J. C.; Melotti, Paola; Sorio, Claudio
Functional rescue of CFTR in rectal organoids from patients carrying R334W variant by CFTR modulators and PDE4 inhibitor Roflumilast 1-gen-2024 Latorre, Roberta Valeria; Calicchia, Martina; Bigliardi, Martina; Conti, Jessica; Kleinfelder, Karina; Melotti, Paola; Sorio, Claudio
Gene Expression Landscape of Chronic Myeloid Leukemia K562 Cells Overexpressing the Tumor Suppressor Gene PTPRG 1-gen-2022 Lombardi, Giulia; Latorre, ROBERTA VALERIA; Mosca, Alessandro; Calvanese, Diego; Tomasello, Luisa; Boni, Christian; Ferracin, Manuela; Negrini, Massimo; Al-Dewik, Nader; A Yassin, Mohamed; Araby, Mohamed; Carpentieri, Bruno; Sorio, Claudio; Lecca, Paola
How the latent geometry of a biological network provides information on its dynamics: the case of the gene network of chronic myeloid leukaemia 1-gen-2023 Lecca, Paola; Lombardi, Giulia; Latorre, Roberta Valeria; Sorio, Claudio
The cereblon E3 ligase modulator, CC-90009, rescues CFTR nonsense variants by promoting NMD suppression and PTC readthrough in rectal organoids 1-gen-2025 Latorre, ROBERTA VALERIA